Search result(s): 15
Kalliopi Sofou,
Kolja Meier,
Leslie E Sanderson,
Debora Kaminski,
Laia Montoliu‐Gaya,
Emma Samuelsson,
Maria Blomqvist,
Lotta Agholme,
Jutta Gärtner,
Chris Mühlhausen,
Niklas Darin,
Tahsin Stefan Barakat,
Lars Schlotawa,
Tjakko van Ham,
Jorge Asin Cayuela,
Fredrik H Sterky
Publication Date:
Article
Pages: 1
Reini E N van der Welle,
Rebekah Jobling,
Christian Burns,
Paolo Sanza,
Jan A van der Beek,
Alfonso Fasano,
Lan Chen,
Fried J Zwartkruis,
Susan Zwakenberg,
Edward F Griffin,
Corlinda ten Brink,
Tineke Veenendaal,
Nalan Liv,
Conny M A van Ravenswaaij‐Arts,
Henny H Lemmink,
Rolph Pfundt,
Susan Blaser,
Carolina Sepulveda,
Andres M Lozano,
Grace Yoon,
Teresa Santiago‐Sim,
Cedric S Asensio,
Guy A Caldwell,
Kim A Caldwell,
David Chitayat,
Judith Klumperman
Publication Date:
Article
Pages: 1
Targeted genome editing in vivo corrects a Dmd duplication restoring wild‐type dystrophin expression
Eleonora Maino,
Daria Wojtal,
Sonia L Evagelou,
Aiman Farheen,
Tatianna W Y Wong,
Kyle Lindsay,
Ori Scott,
Samar Z Rizvi,
Elzbieta Hyatt,
Matthew Rok,
Shagana Visuvanathan,
Amanda Chiodo,
Michelle Schneeweiss,
Evgueni A Ivakine,
Ronald D Cohn
Publication Date:
Article
Pages: 1
Linda Scaramuzza,
Giuseppina De Rocco,
Genni Desiato,
Clementina Cobolli Gigli,
Martina Chiacchiaretta,
Filippo Mirabella,
Davide Pozzi,
Marco De Simone,
Paola Conforti,
Massimiliano Pagani,
Fabio Benfenati,
Fabrizia Cesca,
Francesco Bedogni,
Nicoletta Landsberger
Publication Date:
Article
Pages: 1
Marina Pavlou,
Christian Schön,
Laurence M Occelli,
Axel Rossi,
Nadja Meumann,
Ryan F Boyd,
Joshua T Bartoe,
Jakob Siedlecki,
Maximilian J Gerhardt,
Sabrina Babutzka,
Jacqueline Bogedein,
Johanna E Wagner,
Siegfried G Priglinger,
Martin Biel,
Simon M Petersen‐Jones,
Hildegard Büning,
Stylianos Michalakis
Publication Date:
Article
Pages: 1
Publication Date:
Article
Pages: 1
Development of a small molecule that corrects misfolding and increases secretion of Z α1‐antitrypsin
David A Lomas,
James A Irving,
Christopher Arico‐Muendel,
Svetlana Belyanskaya,
Andrew Brewster,
Murray Brown,
Chun‐wa Chung,
Hitesh Dave,
Alexis Denis,
Nerina Dodic,
Anthony Dossang,
Peter Eddershaw,
Diana Klimaszewska,
Imran Haq,
Duncan S Holmes,
Jonathan P Hutchinson,
Alistair M Jagger,
Toral Jakhria,
Emilie Jigorel,
John Liddle,
Ken Lind,
Stefan J Marciniak,
Jeff Messer,
Margaret Neu,
Allison Olszewski,
Adriana Ordonez,
Riccardo Ronzoni,
James Rowedder,
Martin Rüdiger,
Steve Skinner,
Kathrine J Smith,
Rebecca Terry,
Lionel Trottet,
Iain Uings,
Steve Wilson,
Zhengrong Zhu,
Andrew C Pearce
Publication Date:
Article
Pages: 1
Valentina Vavassori,
Elisabetta Mercuri,
Genni E Marcovecchio,
Maria C Castiello,
Giulia Schiroli,
Luisa Albano,
Carrie Margulies,
Frank Buquicchio,
Elena Fontana,
Stefano Beretta,
Ivan Merelli,
Andrea Cappelleri,
Paola MV Rancoita,
Vassilios Lougaris,
Alessandro Plebani,
Maria Kanariou,
Arjan Lankester,
Francesca Ferrua,
Eugenio Scanziani,
Cecilia Cotta‐Ramusino,
Anna Villa,
Luigi Naldini,
Pietro Genovese
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Article
Pages: 1
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Article
Pages: 1
Hong Wei Yang,
Semin Lee,
Dejun Yang,
Huijun Dai,
Yan Zhang,
Lei Han,
Sijun Zhao,
Shuo Zhang,
Yan Ma,
Marciana F Johnson,
Anna K Rattray,
Tatyana A Johnson,
George Wang,
Shaokuan Zheng,
Rona S Carroll,
Peter J Park,
Mark D Johnson
Publication Date:
Article
Pages: 1