Search result(s): 3
Targeted genome editing in vivo corrects a Dmd duplication restoring wild‐type dystrophin expression
Eleonora Maino,
Daria Wojtal,
Sonia L Evagelou,
Aiman Farheen,
Tatianna W Y Wong,
Kyle Lindsay,
Ori Scott,
Samar Z Rizvi,
Elzbieta Hyatt,
Matthew Rok,
Shagana Visuvanathan,
Amanda Chiodo,
Michelle Schneeweiss,
Evgueni A Ivakine,
Ronald D Cohn
Publication Date:
Article
Pages: 1
Mirko Signorelli,
Mitra Ebrahimpoor,
Olga Veth,
Kristina Hettne,
Nisha Verwey,
Raquel García‐Rodríguez,
Christa L Tanganyika‐deWinter,
Luz B Lopez Hernandez,
Rosa Escobar Cedillo,
Benjamín Gómez Díaz,
Olafur T Magnusson,
Hailiang Mei,
Roula Tsonaka,
Annemieke Aartsma‐Rus,
Pietro Spitali
Publication Date:
Article
Pages: 1
Ning Ran,
Caorui Lin,
Ling Leng,
Gang Han,
Mengyuan Geng,
Yingjie Wu,
Scott Bittner,
Hong M Moulton,
HaiFang Yin
Publication Date:
Article
Pages: 1