Search result(s): 3
Targeted genome editing in vivo corrects a Dmd duplication restoring wild‐type dystrophin expression
Eleonora Maino,
Daria Wojtal,
Sonia L Evagelou,
Aiman Farheen,
Tatianna W Y Wong,
Kyle Lindsay,
Ori Scott,
Samar Z Rizvi,
Elzbieta Hyatt,
Matthew Rok,
Shagana Visuvanathan,
Amanda Chiodo,
Michelle Schneeweiss,
Evgueni A Ivakine,
Ronald D Cohn
Publication Date:
Article
Pages: 1