Search result(s): 3
Targeted genome editing in vivo corrects a Dmd duplication restoring wild‐type dystrophin expression
Eleonora Maino,
Daria Wojtal,
Sonia L Evagelou,
Aiman Farheen,
Tatianna W Y Wong,
Kyle Lindsay,
Ori Scott,
Samar Z Rizvi,
Elzbieta Hyatt,
Matthew Rok,
Shagana Visuvanathan,
Amanda Chiodo,
Michelle Schneeweiss,
Evgueni A Ivakine,
Ronald D Cohn
Publication Date: 16 March, 2021
Article
Pages: 1
Targeted attenuation of elevated histone marks at SNCA alleviates α‐synuclein in Parkinson's disease
Subhrangshu Guhathakurta,
Jinil Kim,
Levi Adams,
Sambuddha Basu,
Min Kyung Song,
Evan Adler,
Goun Je,
Mariana Bernardo Fiadeiro,
Yoon‐Seong Kim
Publication Date: 11 January, 2021
Article
Pages: 1
Stefanie Kurtz,
Andrea Lucas-Hahn,
Brigitte Schlegelberger,
Gudrun Göhring,
Heiner Niemann,
Thomas C. Mettenleiter,
Björn Petersen
Publication Date: 22 December, 2020
Article
Pages: 1